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2010 Senate Appropriations
Hearing on FDA's Review
Process for Rare Diseases |
2010 FDA Hearing on
Rare Diseases |
Dr. Kakkis Featured as a
Rock Star of Science |
What Dr. Kakkis would
say to President Obama |
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Kakkis in the News |
 | | Orphan Drug Advocates Continue Press For Policies Not In PDUFA Pact - InsideHealthPolicy.com - September 12, 2011 | | | EveryLife Pushes New Drug Review Structure As PDUFA Debate Nears - FDA Week - August 19, 2011 | | | Crafting a Robust Business Model for Orphan Drug Development - HUMAN GENE THERAPY - July 01, 2011 | | | Our Hero: The Crusade of Dr. Emil Kakkis '82 to hasten treatment for kids with rare diseases - Pomoma College Magazine - December 31, 2010 | | | Battling Rare Diseases in a Blockbuster World - California Biomedical Industry 2010 Report - December 31, 2010 | | | Novato doctor seeks cures for rare childhood diseases - Marin Independent Journal - December 18, 2010 | | | Dr. Kakkis Featured on the "PERSPECTIVES" PODCAST SERIES, presented by Children's Rare Disease Network. - - November 29, 2010
Click Here to Listen to Emil’s Interview. | | | Former BioMarin exec targets orphan drugs - San Francisco Business Times - October 15, 2010 | | | Dr. Kakkis receives Spirit of Excellence Award from the Los Angeles Biomedical Research Institute - - November 06, 2009 | | | Debate Continues Over Patient Access to Investigational Drugs - Medscape Medical News - November 03, 2009 | | | New FDA Groups For Rare, Neglected Diseases Could Speed Path to Market - The Grey Sheet - October 12, 2009 | | | Harbor-UCLA Pediatrics Alumni Interview with Emil Kakkis, M.D., Ph.D. - Harbor UCLA - October 10, 2009 | | | Patient Group Hopes Tweaks to Approps Bill Lead to New FDA Office - FDA Week - October 09, 2009 | | | Expanded Access Programs Vital, but New Rules Raise Concerns - - October 01, 2009 | | | Dr. Kakkis, First Visiting Scientist of The Manton Center for Orphan Disease Research - - September 09, 2009 | | | Patient Group Seeks New FDA Rare Disorder Office in Approps Bill - FDA Week - August 28, 2009 |
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Foundation Papers, Presentations, Releases & Letters |
| | Dr. Kakkis’ Response to an article on rare cancer published by the Journal of the American Medical Association - - July 07, 2011 | | | The potential investment impact of improved access to accelerated approval on the development of treatments for low prevalence rare diseases - Orphanet Journal of Rare Diseases - July 06, 2011 by B. Miyamoto & Emil Kakkis, MD PhD | | | Dr. Emil Kakkis and 16 Other Rock Stars of Science Paired with 8 Rock Celebrities - in GQ's December “Men of the Year” Issue - November 17, 2010 | | | A Great Win for Rare Diseases in U.S. Senate Appropriation Bill - EveryLife Foundation for Rare Diseases - July 15, 2010 | | | Dr. Kakkis' video presentation at the 11th International Symposium on MPS and Related Diseases, in Adelaide, South Australia - - June 30, 2010- Part 1 - Part 2 - Part 3 | | | "1st Annual EveryLife Art Contest Winners Announced" - EveryLife Foundation for Rare Diseases - March 21, 2010 | | | Foundation taps into JP Morgan Healthcare Conference Attendees to Accelerate Biotech Innovation for Rare Diseases - EveryLife Foundation for Rare Diseases - January 10, 2010 |
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